Nicolas Wein, PhD (Assistant Professor) and his group study the mechanisms of pathogenesis of neuromuscular disorders with a primary focus on Duchenne Muscular dystrophy (DMD) and Dystrophy myotonic type 1 (DM1). The Wein Lab is developing pertinent therapeutic strategy using translational research, an emerging field which can be summarized as understanding the cause of a disease and learning from it in order to develop innovative therapeutic strategies. Our long-term projects focus on RNA and DNA editing and gene transfer as therapies for neuromuscular disorders. In particular, our lab uses the newest technologies, such as virus-mediated exon-skipping (U7snRNA) and the CRISPR/Cas9 genome editing tool. Dr. Wein is also the co-director of the cell line CORT and co-investigator for a number preclinical studies. Lab Members
Florence Robriquet, PhD Postdoctoral Scientist Yacidzohara Rodriguez, PhD Postdoctoral Scientist Molly Giammarco, BS Research Assistant Daniel Lesman, BS Undergraduate Student
Nicolas Wein, PhD (Assistant Professor) and his group study the mechanisms of pathogenesis of neuromuscular disorders with a primary focus on Duchenne Muscular dystrophy (DMD) and Dystrophy myotonic type 1 (DM1). The Wein Lab is developing pertinent therapeutic strategy using translational research, an emerging field which can be summarized as understanding the cause of a disease and learning from it in order to develop innovative therapeutic strategies. Our long-term projects focus on RNA and DNA editing and gene transfer as therapies for neuromuscular disorders. In particular, our lab uses the newest technologies, such as virus-mediated exon-skipping (U7snRNA) and the CRISPR/Cas9 genome editing tool. Dr. Wein is also the co-director of the cell line CORT and co-investigator for a number preclinical studies. Lab Members
Florence Robriquet, PhD Postdoctoral Scientist Yacidzohara Rodriguez, PhD Postdoctoral Scientist Molly Giammarco, BS Research Assistant Daniel Lesman, BS Undergraduate Student
Nicolas Wein, PhD (Assistant Professor) and his group study the mechanisms of pathogenesis of neuromuscular disorders with a primary focus on Duchenne Muscular dystrophy (DMD) and Dystrophy myotonic type 1 (DM1). The Wein Lab is developing pertinent therapeutic strategy using translational research, an emerging field which can be summarized as understanding the cause of a disease and learning from it in order to develop innovative therapeutic strategies. Our long-term projects focus on RNA and DNA editing and gene transfer as therapies for neuromuscular disorders. In particular, our lab uses the newest technologies, such as virus-mediated exon-skipping (U7snRNA) and the CRISPR/Cas9 genome editing tool. Dr. Wein is also the co-director of the cell line CORT and co-investigator for a number preclinical studies. Lab Members
Florence Robriquet, PhD Postdoctoral Scientist Yacidzohara Rodriguez, PhD Postdoctoral Scientist Molly Giammarco, BS Research Assistant Daniel Lesman, BS Undergraduate Student
Nicolas Wein, PhD (Assistant Professor) and his group study the mechanisms of pathogenesis of neuromuscular disorders with a primary focus on Duchenne Muscular dystrophy (DMD) and Dystrophy myotonic type 1 (DM1). The Wein Lab is developing pertinent therapeutic strategy using translational research, an emerging field which can be summarized as understanding the cause of a disease and learning from it in order to develop innovative therapeutic strategies. Our long-term projects focus on RNA and DNA editing and gene transfer as therapies for neuromuscular disorders. In particular, our lab uses the newest technologies, such as virus-mediated exon-skipping (U7snRNA) and the CRISPR/Cas9 genome editing tool. Dr. Wein is also the co-director of the cell line CORT and co-investigator for a number preclinical studies.
Lab Members
- Florence Robriquet, PhD Postdoctoral Scientist
- Yacidzohara Rodriguez, PhD Postdoctoral Scientist
- Molly Giammarco, BS Research Assistant
- Daniel Lesman, BS Undergraduate Student
