Balancing the Known and Unknown Risks and Benefits of Disease Modifying Therapies, Stem Cell Transplantation and Gene Therapy This symposium will provide information to our regional colleagues and our patients and families on current clinical trials and advances in the field of Disease Modifying Therapies (DMT), Stem Cell Transplantation (SCT) and Gene Therapy in Sickle Cell Disease (SCD). The aim of this symposium is to critically analyze and review the pros and cons of these newer treatments including curative options. Topics include:

Living With Sickle Cell Disease What’s New in Matched Sibling Donor (MSD) for SCD Alternative Donor Transplant Options Gene Therapy for SCD

Friday, November 11 – Professional Track Keynote Speakers

Adeltola Kassim, MD, MS, Vanderbilt-Ingram Cancer Center Niketa Shah, MD, Smilow Cancer Hospital at Yale New Haven Wally Smith, MD, Virginia Commonwealth University School of Medicine Mark Walters, MD, University of California, San Francisco

Saturday, November 12 – Family Track The purpose of this half-day session is to provide education to patients and families affected by Sickle Cell Disease. The program will allow us to address family questions about DMTs, stem cell transplant and gene therapy.

Balancing the Known and Unknown Risks and Benefits of Disease Modifying Therapies, Stem Cell Transplantation and Gene Therapy

This symposium will provide information to our regional colleagues and our patients and families on current clinical trials and advances in the field of Disease Modifying Therapies (DMT), Stem Cell Transplantation (SCT) and Gene Therapy in Sickle Cell Disease (SCD). The aim of this symposium is to critically analyze and review the pros and cons of these newer treatments including curative options.

Topics include:

  • Living With Sickle Cell Disease
  • What’s New in Matched Sibling Donor (MSD) for SCD
  • Alternative Donor Transplant Options
  • Gene Therapy for SCD

Friday, November 11 – Professional Track

Keynote Speakers

  • Adeltola Kassim, MD, MS, Vanderbilt-Ingram Cancer Center
  • Niketa Shah, MD, Smilow Cancer Hospital at Yale New Haven
  • Wally Smith, MD, Virginia Commonwealth University School of Medicine
  • Mark Walters, MD, University of California, San Francisco

Saturday, November 12 – Family Track

The purpose of this half-day session is to provide education to patients and families affected by Sickle Cell Disease. The program will allow us to address family questions about DMTs, stem cell transplant and gene therapy.